Comment from Cure GM1 Foundation

Summary: The Cure GM1 Foundation, a nonprofit patient advocacy organization, supports the FDA's Externally Led Patient-Focused Drug Development (EL-PFDD) framework, noting its success in mobilizing their community and creating a "Voice of the Patient" report. They propose improvements such as a structured acknowledgment process for reports, a new joint scientist-caregiver meeting format, and guidance on the lifecycle of patient engagement as drug development progresses.